Bone scan & CT of calcified spleen in sickle cell disease
Biologic and Clinical Efficacy of LentiGlobin for Sickle Cell Disease | One-time treatment with LentiGlobin resulted in sustained production of HbAT87Q in most red cells, leading to reduced hemolysis and complete resolution of severe vaso-occlusive events. nejm.org/doi/full/10.1056β¦
Gene Therapy Is Coming of Age ["researchers have now reported a number of success stories: they have alleviated some cases of blindness, cured cancers, addressed the underlying cause of sickle cell disease, and begun to treat congenital disorders, such as spinal muscular atrophy"] scientificamerican.com/arβ¦
$17 million will launch trial of CRISPR cure for sickle cell disease news.berkeley.edu/2021/12β¦
Girl with sickle cell disease had a wish to be on a billboard. She and her twin now smile at passing cars in Md. washingtonpost.com/lifestβ¦
"Biologic and Clinical Efficacy of LentiGlobin for Sickle Cell Disease", Kanter et al 2021 (sickle cell has been cured) gwern.net/docs/genetics/eβ¦
I have created the Sickle Cell Storytime Series. The goal of this series is to encourage other people suffering from sickle cell and other chronic illnesses to share their stories in order to provide more education for the disease state, spread awareness, and inspire others to share their stories. youtube.com/watch?v=ji7LQβ¦
Update: Statement on NHLBI decision to resume participant enrollment in the Pilot and Feasibility Study of Hematopoietic Stem Cell Gene Transfer for Sickle Cell Disease nhlbi.nih.gov/education-aβ¦
$GBT ... FDA Approves Supplemental New Drug Application for Expanded Indication of Oxbryta (voxelotor) for Children as Young as 4 Years of Age with Sickle Cell Disease
FDA Approves Supplemental New Drug Application for Expanded Indication of Oxbryta (voxelotor) for Children as Young as 4 Years of Age with Sickle Cell Disease!
S. 3389: A bill to amend title XIX of the Social Security Act to establish a demonstration project to improve outpatient clinical care for individuals with sickle cell disease.
Introduced: Sponsor: Sen. Cory Booker [D-NJ]
This bill was referred to the Senate Committee on Finance which will consider it before sending it to the Senate floor for consideration.
1 cosponsor is on that committee.
UCSF Benioff Childrenβs Hospital Oakland receives $17 million to find a cure for sickle cell disease sfchronicle.com/health/arβ¦
Sickle cell disease inquiry finds βserious care failingsβ in NHS Report by cross-party MPs also finds evidence of attitudes underpinned by racism theguardian.com/society/2β¦
The most common cause of osteomyelitis in sickle cell disease?
I keep seeing conflicting info on this. Some say salmonella and some say staph aureus. Which one would be correct when both are present as answer choices in a question?
Ledley King giving blood to aid the fight against sickle cell disease at our stadium today ππ€
A point-of-care, low-cost device called Gazelle β thatβs both portable and easy to use β can accurately diagnose sickle cell disease (SCD) in less than 15 minutes, according to a study done in India sicklecellanemianews.com/β¦
Five Tips For Managing Sickle Cell Disease! Hope sickle cell warriors find this video helpful. Have a blessed day! youtu.be/Lgiq5o-fmgA
$BEAM - *Beam Therapeutics: FDA Clears BEAM-101 IND for Evaluation as Treatment for Sickle Cell Disease
CRISPR-Cas9 gene editing successful for a patient with Sickle Cell Disease and another patient with transfusion dependent Ξ²-Thalassemia - More than a year later, both patients had clinically improved and no longer needed blood transfusions. (NEJM, 5 Dec 2020) nejm.org/doi/full/10.1056β¦
FDA Approves Supplemental New Drug Application for Expanded Indication of Oxbryta (voxelotor) for Children as Young as 4 Years of Age with Sickle Cell Disease
$GBT ... FDA Approves Supplemental New Drug Application for Expanded Indication of Oxbryta (voxelotor) for Children as Young as 4 Years of Age with Sickle Cell Disease.
FDA Approves Supplemental New Drug Application for Expanded Indication of Oxbryta (voxelotor) for Children as Young as 4 Years of Age with Sickle Cell Disease
